The Revell family hoped a gene therapy could buy time for their sons, who have a rare and fatal disease. After two patients ...

The Carolinas rank among the worst in the country for sexual transmitted disease cases, according to a new report.

A study evaluating a pioneering lentivirus (LV)-mediated gene therapy trial for classical Fabry disease showed promising ...

A new report from Invigor Medical analyzing data from the Centers for Disease Control and Prevention’s National Center for ...

According to a recent analysis by Invigor Medical, Georgia recorded the fourth-highest rate of newly reported STD cases in ...

As the future of rare disease research at Cincinnati Children's is threatened, parents of 13-year-old Charlie Evans plead for its reinstatement.

The mother of a nine-year-old British Columbia girl with a rare and deadly disease says she's "disgusted" with the decision not to renew coverage for medication that costs about $1 million a year.

Outrunning Rare Diseases with Coca added by Sierra Lidén on July 11, 2025 View all posts by Sierra Lidén → You must be logged in to post a comment Login ...

A key lawmaker and Florida State University leaders Wednesday touted a new law that includes offering free genetic screening for newborns and bolstering research on rare pediatric diseases. Gov ...

A Utah woman is sharing her story after she survived an incredibly rare and often fatal skin disorder caused by an allergic reaction to antibiotics.

Although each rare disease affects only a small number of people, over 6,000 rare diseases have been identified—so all together these diseases are a major burden for many patients and their families.

Hundreds of parents were notified via letter from the Australian government that their kids should be tested for infectious diseases ...