The trial consisted of two parts: Part A, a randomized and placebo-controlled segment in healthy adult male volunteers and Part B, an open-label segment in pediatric participants with SMA who ...

Ionis Pharmaceuticals, Inc. (Nasdaq: IONS) today announced that its partner, Biogen, shared positive topline results from the Phase 1 study of salanersen (IO ...

Biogen licensed the global development, manufacturing and commercialization rights for salanersen from Ionis Pharmaceuticals, Inc. Salanersen was discovered by Ionis. About Spinal Muscular Atrophy ...

Amy came in earlier this week wanting to make a big change in her life that we tried to talk her out of. Did she listen to us or did she do it anyway? Bobby shared an awesome trick you can do in ...

According to senior sources, the Liberal Party’s failure to reflect the demographics of the country has made its chance of re ...

A commercial Limousin cross heifer named ULucky triumphed in the sun at Fettercairn Show, leading a field of standout livestock champions.

When the top spotty fish in a tank disappears, the runner-up turns aggressive within minutes, rushing and nipping rivals ...

In animals with social structures, the drive to reproduce is a complex process; governed by the brain, it's influenced by ...

Differences in income between male and female academic physicians are well known, but differences for community physicians and career differences in income have not been quantified. We used ...

Birds have developed a unique evolutionary solution to ensure the survival of males – a powerful microRNA. This tiny gene allows male embryos to survive despite a genetic imbalance between the sexes ...

The higher dose regimen of nusinersen comprises a more rapid loading regimen – two 50 mg doses 14 days apart – and a higher maintenance regimen – 28 mg every four months. “As the SMA treatment ...