AstraZeneca said on Thursday its experimental therapy, gefurulimab, met the primary goal and all secondary endpoints in a ...

Meet 12 biotech companies with promising genetic disease therapies that successfully closed funding rounds recently.

Rare diseases impact millions, yet most lack treatment options. This post explores the inequities rare disease patients face and the urgent need to accelerate access to life-changing medicines.

There are approximately 7,000 different types of rare disease and researchers estimate that there are more than 300 million people worldwide living with such a condition, according to the National ...