When 15-month-old Nora received her diagnosis, no one could have predicted the impact it would have on her sister Kayla.

The Revell family hoped a gene therapy could buy time for their sons, who have a rare and fatal disease. After two patients died, the drug’s manufacturer halted dosing under pressure from the FDA.

Obesity increases the risk of nearly 200 diseases. A new genetic test may be able to predict a young child's risk of obesity in adulthood.

Complex regions of the human genome remained uncharted, even after researchers sequenced the genome in its entirety. That is, ...

An antibody treatment developed at Stanford Medicine successfully prepared patients for stem cell transplants without toxic ...